New Scientist

Unapproved gene therapy for boosting longevity is set to go on sale

A gene therapy that instructs cells to produce more of an anti-ageing protein called klotho is about to be offered by a US ...
Medical Xpress

New route into cells could make gene therapies safer

Scientists from the Centenary Institute and the University of Sydney have made a landmark discovery that could lead to safer and more effective gene therapies for a range of serious genetic disorders ...
Nature

Advancing the Integration of ‘Basic/Fundamental’ and Translational Cellular and Gene Therapy Science within the EBMT: Accelerating the Pathway to Progress

The mission statement of the EBMT is to function as ‘a community of healthcare professionals focused on innovation, research and the advancement of cellular and stem cell-based therapies to save and ...
BioProcess International

Integrating Quality by Design Principles into Gene-Therapy CMC Programs: Establishing Manufacturing Control and Comparability

Quality by design is critical for cell and gene therapy manufacturing where process controls directly influence product ...
CNN

The race is on to turn your body into a GLP-1 factory

People looking to lose weight and lower their blood sugar may someday be able to get a single injection that turns their cells into tiny factories churning out a protein that is essentially the active ...
Forbes

A Turning Point For Gene Therapy: What One Tragic Event Reveals About The Promise And Peril Of Genetic Medicine

Forbes contributors publish independent expert analyses and insights. A patient in a late-stage gene editing trial for a rare heart condition died from fatal liver complications after receiving an ...
Medscape

Gene Therapy Injections for Knee OA: Where Are We At?

The idea behind intra-articular gene therapy for treating osteoarthritis (OA) is to deliver the gene-altering vector or cells directly to the precise site of the disease with a single injection — so ...

Israeli hospital performs world's first experimental gene therapy for rare genetic epilepsy

The treatment, administered at Schneider Children’s Medical Center of Israel in Petah Tikva, is a major milestone in the ...

First-in-the-world gene therapy delivers missing gene directly to infant's brain

An 8-month-old infant with severe genetic epilepsy has become the first patient in the world to receive an experimental gene ...
Science Daily

Deafness reversed: One injection restores hearing in just weeks

A new gene therapy is giving people born deaf the chance to hear, often within just weeks. In a small but groundbreaking study, researchers delivered a working copy of a key hearing gene directly into ...
Nature

Gene therapy for cardiac arrhythmias

Cardiovascular diseases are the leading cause of death globally, with cardiac arrhythmias contributing substantially to this burden. Gene therapy, which directly targets the underlying disease ...

First-in-the-World Gene Therapy Delivers Missing Gene Directly to Infant's Brain, Marking Historic Milestone in Precision Medicine

An eight-month-old infant with a severe genetic epilepsy has become the first patient in the world to receive an experimental gene replacement therapy designed to restore the function of the WWOX gene ...