Healio

Q&A: Advocates meet with lawmakers in support of patients with Friedreich’s ataxia

Limited treatment options and access to care often challenge patients with Friedreich’s ataxia. So, on Sept. 17, the ...
The Healthy @Reader's Digest

Bill Nye the Science Guy Shares the #1 Health Habit He Follows “All the Time”

"I don't know if you've heard about it," says the long-adored scientist and climate activist—plus, the one rising condition that tells him "there's something going on." ...

Receptor in cerebellum provides new insights into molecular basis of ataxia

Researchers at Ruhr University Bochum, Germany, identified a receptor that plays a crucial role in stress-induced motor ...

Late-onset cerebellar ataxia: A genetic avenue uncovered

Could an anomaly in the developing brain explain motor difficulties occurring decades later in people with rare movement ...
STV News

'My rare disease is getting worse - I want more time to play with my children'

Daniel Fraser, 36, was diagnosed with Friedreich’s Ataxia, a progressive disease that causes mobility, speech issues and ...

Quince Therapeutics Presents Data from Patient-Reported Walking Capacity in Children with Ataxia-Telangiectasia at 54th Child Neurology Society Annual Meeting

Quince Therapeutics, Inc. (Nasdaq: QNCX), a late-stage biotechnology company dedicated to unlocking the power of a patient’s ...

Lexeo climbs after regulatory update on Friedreich ataxia drug

Lexeo Therapeutics (LXEO) stock rises as the FDA supports a potential accelerated approval pathway for LX2006, its treatment for Friedreich ataxia. Read more here.
BioWorld

Lexeo and FDA position Friedreich ataxia therapy for accelerated approval

Lexeo Therapeutics Inc. feels like it’s in a faster lane to a BLA for its Friedreich ataxia cardiomyopathy therapy after a talk with the U.S. FDA. The agency told Lexeo that LX-2006 could be on the ...