Treatment with Spinraza (nusinersen) can help stabilize or improve motor function in adults with SMA, according to a new ...
Over 95% of babies now diagnosed with SMA are treated with Zolgensma gene therapy, per Daniel Grant, vice president for ...
In the last of a series, columnist Sherry Toh shares how she's coping with an intense leg of her journey with chronic pain ...
After facing several damaging storms, columnist Helen Baldwin was delighted to see a daffodil blooming amid the chaos.
The muscle-strengthening therapy apitegromab is being considered for approval by the U.S. Food and Drug Administration (FDA) as an add-on treatment for spinal muscular atrophy (SMA), with a decision ...
Activating a protein called potassium channel Kv2.1 may help improve motor function in SMA, making it a potential SMA ...
Activating a protein called potassium channel Kv2.1 may help improve motor function in SMA, making it a potential SMA ...
A higher dose of Spinraza may be more effective than the currently approved dosing schedule for maintaining motor function in ...